Episode 388: #90-3 Pediatric Neurology: Gene Therapy

In this episode of our pediatric neurology series, host Paul Wirkus, MD, FAAP and guest Josh Bonkowsky, MD explore the rapidly evolving field of gene therapy and its potential to transform the care of children with neurologic disorders. Our guest explains the science behind gene therapy, including how these treatments work to target the underlying causes of genetic disease.

The conversation also examines emerging approaches to gene editing and the exciting possibilities these technologies hold for the future of pediatric medicine. Alongside the promise of these innovations, we discuss the challenges, ethical considerations, and unanswered questions that accompany this new era of precision medicine.

Throughout the episode, our guest emphasizes the importance of helping patients and families understand complex treatment options so they can make informed decisions as the landscape of genetic diagnosis and therapy continues to evolve.

Have a question? Email [email protected]. Listener questions will be answered in episode four. For more information about available credit, visit vCurb.com.ACCME Accreditation StatementThis activity has been planned and implemented in accordance with the accreditation requirements and policies of the Colorado Medical Society through the joint providership of Kansas Chapter, American Academy of Pediatrics and Utah Chapter, AAP. Kansas Chapter, American Academy of Pediatrics is accredited by the Colorado Medical Society to provide continuing medical education for physicians. AMA Credit Designation StatementKansas Chapter, American Academy of Pediatrics designates this live activity for a maximum of 1.0 AMA PRA Category 1 Credits™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.